Get to Know The Kids with AGU

Many children around the world are living with ultra-rare diseases. Meet Daniel, Alexander, Hermance, Trisha, Makeda, George, Sydney, Selman, and Jor—each diagnosed with Aspartylglucosaminuria (AGU) and in urgent need of a cure.

Click the links below to get to know these incredible kids and learn how you can help bring hope through gene therapy.