with your Support there is Hope

Your donation directly supports research, gene therapy development, drug production, and clinical trials to help children living with Aspartylglucosaminuria (AGU).

This life-saving work is only possible because of the generosity, compassion, and dedication of people like you.

Whether large or small, every contribution makes a real difference in the lives of children affected by this ultra-rare disease.

Thank you for being part of the cure.